Tag: Hemophilia
ASH: High-Dose Gene Transfer Beneficial in Severe Hemophilia A
Factor VIII gene transfer tied to sustained normalization of factor VIII activity levels
Gene Therapy Shows Beneficial Effect in Men With Hemophilia B
Reduction in annualized bleeding rate and in factor use with infusion of viral vector with transgene
FDA OKs Drug for Hemophilia A With Factor VIII Inhibitors
Weekly prophylactic treatment associated with substantial decrease in bleeding episodes
Prophylaxis Linked to Improved Function, HRQoL in Hemophilia
Improved function, QoL, activity, pain but not joint structure in adults with hemophilia with joint disease
ASH: Single Dose of Gene Therapy Effective in Hemophilia B
Small, preliminary trial suggests it may free hemophilia B patients from transfusions
New Findings Offer Hope for Those With Severe Hemophilia
One study pinpoints when standard therapy works best; another uncovers the promise of a new drug
Hemophilia Drugs a Big Part of State Medicaid Spending
California-based researchers find medications for childhood hemophilia take up large share of budget
